‘Tremendous leap forward’ – siRNA therapy reduces the burden of disease in haemophilia

Monthly subcutaneous prophylaxis with the small interference RNA (siRNA) therapeutic fitusiran can significantly reduce bleeding in people with haemophilia A or B. Speaking in a plenary scientific session at ASH 2021, Dr Guy Young said that patients with inhibitors typically do poorly compared to other people with haemophilia. Dr Young, director of the Haemostasis and ...

Already a member?

Login to keep reading.

© 2022 the limbic