A new small study has bolstered hopes gene therapy could offer a single-injection cure for haemophilia B. On Tuesday, clinical haematologist and pathologist Professor John Rasko presented an abstract to the HAA conference with top-line results from his recent phase I-II clinical trial of a new adeno-associated virus gene therapy in haemophilia B patients. The ...
Cure for haemophilia B on the horizon?
By Tessa Hoffman
31 Oct 2017