A study exploring the use of the oral drug ivacaftor in very young children with a CFTR gating mutation suggests there may be a window in early life where at least partial restoration of pancreatic function might be possible. The open label single-arm study of 34 pre-school children with cystic fibrosis aged between 2 and ...
Window of opportunity for children with CF
By Nicola Garrett
28 Jan 2016