Novel therapies promise long-term control of haemophilia

The durability of gene transfer for severe haemophilia A is looking encouraging with results now in on the three-year follow-up of patients who received a single dose of valoctocogene roxaparvovec. Professor John Pasi, from the Royal London Hospital Haemophilia Centre, told the ISTH Congress that all patients in the phase 1/2 study had previously shown ...

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