Gene therapy to transform haemophilias: a single infusion reduces bleeding risk

Gene therapy for haemophilia is almost within reach and will be the flagship for the management of other monogenic disorders, according to a keynote speaker at ASH 2019. Delivering the prestigious Ham-Wasserman Lecture, Professor Amit Nathwani said if gene therapies can’t be made to work for haemophilia, the technology was unlikely to work elsewhere.  “The ...

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